Impact of phase II trials with progression-free survival as end-points on survival-based phase III studies in patients with anaplastic gliomas
2007

Impact of Phase II Trials on Survival in Anaplastic Gliomas

Sample size: 529 publication Evidence: high

Author Information

Author(s): Levin Victor A, Ictech Sandra, Hess Kenneth R

Primary Institution: The University of Texas M. D. Anderson Cancer Center

Hypothesis

Is progression-free survival (PFS) an appropriate end-point for phase II trials for anaplastic gliomas and how does it impact phase III trials?

Conclusion

Progression-free survival is a more reliable end-point than overall survival for evaluating chemotherapy effectiveness in patients with anaplastic gliomas.

Supporting Evidence

  • PFS rates at 6, 9, and 12 months were significantly different between treatment groups.
  • 80% of patients at recurrence had a 23% likelihood of living more than 1 year with each chemotherapy.
  • Age and treatment group membership were significant factors affecting PFS.

Takeaway

This study shows that measuring how long patients live without their cancer getting worse is a better way to see if a treatment works than just looking at how long they live overall.

Methodology

Data from 16 phase II studies were combined and analyzed to assess progression-free survival at 6, 9, and 12 months.

Potential Biases

Potential bias due to the retrospective nature of the data collection and exclusion criteria.

Limitations

The study excluded patients with anaplastic ependymoma and those with AOs, which may limit the generalizability of the findings.

Participant Demographics

Patients included were diagnosed with anaplastic gliomas, with a mean age of approximately 41 years and a Karnofsky performance score of around 84.

Statistical Information

P-Value

p<0.0001

Statistical Significance

p<0.0001

Digital Object Identifier (DOI)

10.1186/1471-2407-7-106

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