PPP2R5D-Related Neurodevelopmental Disorder and Multiple Haemangiomas: A Novel Phenotypic Trait?
2024

PPP2R5D-Related Neurodevelopmental Disorder and Multiple Haemangiomas

Sample size: 1 publication Evidence: low

Author Information

Author(s): Comisi Francesco, Soddu Consolata, Lai Francesco, Marica Monica, Lorrai Michela, Mancuso Giancarlo, Giglio Sabrina, Savasta Salvatore

Primary Institution: University of Cagliari

Hypothesis

Is there a link between PPP2R5D-related disorder and multiple haemangiomas?

Conclusion

This study suggests a possible link between PPP2R5D-related disorder and altered angiogenesis, indicating that diffuse haemangiomas may be a novel phenotypic trait of this condition.

Supporting Evidence

  • The patient exhibited multiple haemangiomas and developmental delays.
  • Whole Exome Sequencing confirmed a pathogenic variant in the PPP2R5D gene.
  • The findings suggest a potential link between PPP2R5D dysfunction and angiogenesis.

Takeaway

This study talks about a child with a rare genetic disorder who also has multiple birthmarks called haemangiomas, suggesting they might be related.

Methodology

Whole Exome Sequencing was used to identify a de novo missense variant in the PPP2R5D gene.

Limitations

The study is based on a single case report, limiting the generalizability of the findings.

Participant Demographics

A 1-year-old child born to non-consanguineous parents.

Digital Object Identifier (DOI)

10.3390/pediatric16040101

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