Melarsoprol Cyclodextrin Inclusion Complexes as Promising Oral Candidates for the Treatment of Human African Trypanosomiasis
2011

Oral Treatment for Sleeping Sickness Using Melarsoprol Cyclodextrin Complexes

Sample size: 6 publication 10 minutes Evidence: high

Author Information

Author(s): Rodgers Jean, Jones Amy, Gibaud Stéphane, Bradley Barbara, McCabe Christopher, Barrett Michael P., Gettinby George, Kennedy Peter G. E.

Primary Institution: University of Glasgow

Hypothesis

Can melarsoprol cyclodextrin inclusion complexes be an effective oral treatment for human African trypanosomiasis?

Conclusion

Melarsoprol cyclodextrin complexes are effective in curing CNS-stage human African trypanosomiasis when administered orally.

Supporting Evidence

  • Melarsoprol cyclodextrin complexes were orally effective and non-toxic in curing CNS-stage trypanosome infections in mice.
  • Parasite load within the brain was significantly reduced following treatment.
  • Restoration of blood-brain barrier integrity was observed after treatment.

Takeaway

Researchers found a new way to give a medicine for a serious disease that usually needs a painful injection, and it worked well in mice.

Methodology

The study used in vitro and in vivo methods to test the efficacy of melarsoprol cyclodextrin complexes in mice infected with T.b. brucei.

Limitations

The study was conducted in a murine model, and results may not directly translate to human patients.

Participant Demographics

Female CD-1 mice (20–30 g body weight) were used in the study.

Statistical Information

P-Value

p=0.019

Confidence Interval

95% confidence interval 0.213 g, 1.954 g

Statistical Significance

p<0.05

Digital Object Identifier (DOI)

10.1371/journal.pntd.0001308

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